Orphan drugs, often referred to as the pharmaceutical underdogs, are medications developed to treat rare diseases that affect a small number of individuals. These conditions, termed orphan diseases, typically lack attention and funding due to their limited prevalence, making them commercially unattractive for large pharmaceutical companies.
The term "orphan" in this context doesn't denote the drugs' efficacy but rather the economic challenge of developing treatments for small patient populations. To incentivize research and development in this crucial area, governments often provide incentives such as extended market exclusivity and tax credits. The significance of orphan drugs lies in their ability to bring hope to individuals facing conditions that might otherwise lack effective treatments. By addressing rare diseases, these drugs contribute to a more inclusive and compassionate healthcare landscape, emphasizing the importance of providing solutions for all, regardless of the rarity of their medical conditions.
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Consolato M Sergi, Universities of Alberta and Ottawa, Canada
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Axel H Schonthal, University of Southern California, United States
Title : From marker to mechanism: Ligand discovery enables functional analysis of OR51E1, an ectopic olfactory receptor, in prostate cancer
Vladlen Slepak, University of Miami, United States
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Paulo Cesar De Morais, Catholic University of Brasilia, Brazil
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Bernd Blobel, University of Regensburg, Germany
Title : Personalized and Precision Medicine (PPM) as a unique healthcare model based on design-inspired biotech- & biopharma-driven applications to secure the human healthcare and biosafety
Sergey Suchkov, N D Zelinskii Institute for Organic Chemistry of the Russian Academy of Sciences & InMedStar, Russian Federation
Title : R&D consultancy at the medicines discovery catapult: De-risking drug discovery for innovators
Adriana Gambardella, Medicine Discovery Catapult, United Kingdom
Title : Biocompatible synthesis of non crystalline iron oxide nanoparticles with stable colloidal properties
Lan Wang, Paretor LLC, United States
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Madhav Bhatia, University of Otago, New Zealand
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Luis Jesus Villarreal Gomez, Universidad Autónoma de Baja California, Mexico