Orphan drugs, often referred to as the pharmaceutical underdogs, are medications developed to treat rare diseases that affect a small number of individuals. These conditions, termed orphan diseases, typically lack attention and funding due to their limited prevalence, making them commercially unattractive for large pharmaceutical companies.
The term "orphan" in this context doesn't denote the drugs' efficacy but rather the economic challenge of developing treatments for small patient populations. To incentivize research and development in this crucial area, governments often provide incentives such as extended market exclusivity and tax credits. The significance of orphan drugs lies in their ability to bring hope to individuals facing conditions that might otherwise lack effective treatments. By addressing rare diseases, these drugs contribute to a more inclusive and compassionate healthcare landscape, emphasizing the importance of providing solutions for all, regardless of the rarity of their medical conditions.
Vladlen Slepak
University of Miami School of Medicine, United States
Axel H Schonthal
University of Southern California, United States
Bernd Blobel
University of Regensburg, Germany
Consolato M Sergi
University of Alberta, Canada
Luis Jesus Villarreal Gomez
Universidad Autónoma de Baja California, Mexico
Lan Wang
Paretor LLC, United States
Maria Cristina Gamberini
University of Modena e Reggio Emilia, Italy
Lucas Amaral Machado
University of Sao Paulo State – UNESP, Brazil
Saad Tayyab
UCSI University, Malaysia
Anil Pareek
Anand Pharmacy College, IndiaSubmit your abstract Today
Title : Development of novel drug delivery pathways enabled by perillyl alcohol (NEO100), A monoterpene with multifaceted biomedical applications
Axel H Schonthal, University of Southern California, United States
Title : From marker to mechanism: Ligand discovery enables functional analysis of OR51E1, an ectopic olfactory receptor, in prostate cancer
Vladlen Slepak, University of Miami School of Medicine, United States
Title : Hepatotoxic botanicals-shadows of pearls
Consolato M Sergi, University of Alberta, Canada
Title : Tailored cellular environments to enable drug design
Lan Wang, Paretor LLC, United States
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Bernd Blobel, University of Regensburg, Germany
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Lan Wang, Paretor LLC, United States
Title : Design and characterization of gum arabic buccal films for protein drug delivery
Krisztian Pamlenyi, University of Szeged, Hungary
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Madhav Bhatia, University of Otago, New Zealand